参考文献如下

1.Birnkrant et al. Lancet Neurol. 2018. Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and neuromuscular, rehabilitation, endocrine, and gastrointestinal and nutritional management

2.Duan et al. Nature Reviews Disease Primers. 2021. Duchenne muscular dystrophy

3.Erkut et al. International Journal of Molecular Sciences. 2022. CRISPR Therapeutics for Duchenne Muscular Dystrophy